In Vivo Pharmacology Services

Integrated in vivo pharmacology services (PK/PD/Tox, efficacy and immunohistology) to evaluate diverse therapeutic modalities, supporting preclinical studies, IND filing and beyond

In Vivo Pharmacology Services

Integrated In Vivo Pharmacology Services • Pharmacokinetics (PK) and pharmacodynamics (PD) • Efficacy • Toxicology • Immunohistology

With experience spanning over 800 projects, WuXi Biologics offers integrated, end-to-end in vivo pharmacology services across diverse therapeutic modalities, including monoclonal and bispecific antibodies, ADCs, fusion proteins, and CAR-T therapies. Our deep expertise in key therapeutic areas such as oncology, autoimmune diseases, inflammatory disorders, and diabetes ensures streamlined support from preclinical studies through IND filing and beyond.

In Vivo and Ex Vivo Capabilities

Efficacy Study

Our in vivo and ex vivo capabilities encompass multiple species, extensive PK/PD/Tox studies, and a broad array of efficacy models, delivering actionable insights into mechanism of action (MOA), distribution, and drug candidate efficacy to accelerate your biologic drug projects.

G4 Ab2 3mg/kg G5 Ab2 0.5mg/kg

G1 Control 3mg/kg G2 Ab1 3mg/kg G3 Ab1 0.5mg/kg

10e+06 10e+05 10e+07 10e+08 10e+09 10e+10 10e+11 10e+12 0.1 1 10 100 1000 10000 100000

Tumor-Luciferase Reporter

In Vivo Efficacy Study Models

PK, PD, and Exploratory Toxicity

Multiple Species

Days Post Grouping 0 3 6 9 121518212427

• Mouse, rat and monkey • PK, PD, IHC

• Syngeneic

Rodent PK Study

Humanized/WT • CDX; CDX/PBMC • GVHD • Autoimmunity • Rare disease • Metabolic disease

• In vivo imaging and bio-distribution • In vitro , ex vivo biomarker and MOA studies

Ab1 10 mg/kg Ab3 10 mg/kg Ab2 10 mg/kg

Organ Distribution Analysis

0

3

6

9

12

15

IHC Staining

Time (day)

Holistic PK, PD, and Toxicity Studies

• Rapid response: Monkeys scheduled within 7 days • Highly customized assay development • Flexibility: Adaptable to specific client requirements • Data interpretation: Insightful analysis for integrated projects • Total timeline: 6–11 weeks PK, PD, and Toxicity Service Features

Our comprehensive PK, PD, and toxicity studies include multi-species screening, a dose-concentration-response evaluation, and a determination of safe dosage levels, facilitating leads optimization and supporting every stage of drug development, from early discovery to IND filing.

PK

PD

Tox

Immunophenotyping

Cytokine Analysis

Hematology

TCE-2_(1) TCE-2_(10)

0.1 1 10 100 1000

30 40

150

1000 2000 3000 4000

WBC#

TCE-2 1 mg/kg TCE-2 10 mg/kg

TNF

0 5.58 10 20 26.6

100

p

50

Day-3 0

-72h 1h 2h 4h 8h 24h 144h 0

Time (Day) 0 1 2 3 4 5 6 7

Bio-distribution

TA-12, 15 mg/kg, Male TA-12, 15 mg/kg, Female Receptor Occupancy

Histology

0 20 40 60 80 100

Stained inflammatory cells

0 7 1421 283542 Days a er the treatment

-1

Extensive Efficacy Model Collections

29 Autoimmune Disease Modes

15 Syngeneic Models

87 CDX (PBMC) Models

27 IVIS Imaging Models

7 Metabolism Models

Immunology & Metabolism

Oncology

*Build engineered cell-lines and establish new models on demand

Comprehensive Immunohistology Capabilities

• Comprehensive panel of staining methods: Includes HE, IHC, IF, EHC, and TCR • In-depth tissue analysis: Target evaluation, antibody distribution, immune cells infiltration, and more • Qualified pathology analysis

T Cell Infiltration

Tumor Antigen IHC for Model Characterization & Selection

HE Staining

PBS

mAb1

mAb2

Relative Quantification

***

***

50

Lung Lung

40

High expression High expression

Medium expression Medium expression

Low expression Low Expression

Kidney

30

Multiplex IF for Immuno-Profiling

20

10

0

PBS

mAb1

mAb2

DAPI

hCD4

hCD8

Merged

Case Study 1: Single-Source Solution for In Vivo Characterization of TCE

In this case study, the PK of TCEs was evaluated in vivo . The dose-concentration-response relationship for efficacy was also determined using a cell-derived xenograft (CDX) and peripheral blood mononuclear cells (PBMC) model designed based on tumor target validation through immunohistochemistry (IHC).

Customized PK Platform for TCE

CDX/PBMC Efficacy Model for TCE NCI-H524 in NDG-hPBMC

Biotin

TCE-1 Fc+Fc TCE-1 CD3+Fc

1000

PBS B (0.54 mg/kg) B (0.18 mg/kg) B (0.06 mg/kg) A (0.36 mg/kg) A (0.12 mg/kg) A (0.04 mg/kg) W (0.45 mg/kg) W (0.15 mg/kg) W (0.05 mg/kg)

1000 1500 2000 2500

100

Fc-Fc

Target validation

10

• Customized PK platform: Enables precise measurement of total IgG and TCE levels • Validated CD3 antigen: Ensures specificity and efficacy • Rationally designed CDX and PBMC efficacy model: Supported by target validation to enable potent PBMC donor screening Case Study 2: Established hFcRn Mouse Model for Early-Stage Fc Engineering Assessment 0 7 14 1 Time (Day) CD3-Fc 0 7 14 0 500 Days aer treatment

21

In this case study, we use a well-established hFcRn mouse model to assess Fc engineering at an early stage and simulate the in vivo PK profiles of both human mice and non-human primates (NHPs). • Enhanced PK profiles: An Fc-engineered antibody shows improved PK compared to its wild-type counterpart. • Strong linear correlation in t1/2: A consistent t1/2 correlation was observed between hFcRn and NHP models.

PK Curve of hFcRn Mice IV Infusion

Linear Simulation of t 1/2 Between hFcRn Mice and NHP

5 10 15 20 25

Pearson’s r = 0.91; P < 0.001

1000

G1_Wt t1/2=113 G2-Fc Engineered t1/2=260h

100

10

1

5

10

15

20

25

0.1

hFcRn mice half life (days)

0

7

14

21

Time (Day)

Valente et al; mAbs; 2020, VOL. 12, NO. 1, 13

About WuXi Biologics

WuXi Biologics is a leading contract research, development, and manufacturing organization (CRDMO) that provides end-to-end capabilities to healthcare organizations worldwide. With operations in China, the United States, Ireland, Germany, and Singapore, we enable our partners to effectively and efficiently bring biologics and vaccines to patients worldwide through our comprehensive and high-quality drug development model.

The world’s leading global single-source platform from concept to commercialization

wuxibiologics.com | PS_BD@wuxibiologics.com

12-3-2024

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